Will Pfizer’s muscular dystrophy gene therapy cross the finish line?

Others have tried and failed — could this one yield a happy ending for patients?

Image via Unsplash

In early 2021, a young boy in Barcelona was the first to receive Pfizer’s investigational gene therapy for Duchenne muscular dystrophy (DMD). This was part of a global Phase 3 human trial to test Pfizer’s lead candidate, PF-06939926, in a cohort of 99 patients with…



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River D'Almeida, Ph.D

Follow me for bite-sized stories on the latest discoveries and innovations in biomedical research.